Congratulations to all of the recipients, including katia aquilano, @Cherqui_S, and USF Health Together, we will #SlowStopReverse and #CureFA

Professor Stephanie Cherqui of UC San Diego School of Medicine speaks to us about a prestigious grant from the California Institute for Regenerative Medicine, which will allow her team to bring a new CRISPR therapy for Friedreich’s ataxia to the clinic. Read more here: bit.ly/3WxA2nV

Excited to share the FAID reel of 2022! It's a delightful visual summary of our recent conference. Our team has worked hard to make this event happen, and we couldn't be more proud of what we have achieved so far. #ClinicalTrials #GeneTherapy france-science.com/en/france-and-…

I am very happy and grateful to have received the fellowship award from the Cure Sanfilippo Fdn to continue my work investigating the use of #stemcell #genetherapy to treat Sanfilippo type C in the Cherqui Lab UC San Diego Health

Thank you Rafael A. Badell-Grau, PhD for representing our lab at WORLDSymposia 2023. Also, a special acknowledgement goes out to National MPS Society and Cure Sanfilippo Fdn for your fellowship supports!

🎧 NEW PODCAST 🎧 Professor @Cherqui_S is a pioneer in the field of #CRISPR cell and gene therapies. She speaks about her work on curing genetic diseases such as Friedreich's ataxia, obstacles in clinical development, and the future of CRISPR therapies 👉 hubs.li/Q01HM8kb0

Happy to be back presenting a poster at the ASGCT annual meeting on my work at Cherqui Lab on #stemcell #GeneTherapy for Sanfilippo C funded by National MPS Society & Cure Sanfilippo Fdn. Poster No. 649

Great week for the Cherqui lab ⁦ASGCT⁩ presenting our latest work! #stemcell #genetherapy ⁦UC San Diego Health⁩ linkedin.com/posts/stephani…

Honoured to have been awarded one of the ASGCT 2023 outstanding poster award for my abstract on my work in the Cherqui Lab UC San Diego Health on Hematopoeitic #stemcell #genetherapy for MPSIIIC funded by National MPS Society & Cure Sanfilippo Fdn

EXCITING STUDY! In new proof-of-concept study, Priyanka Mishra, Stephanie Cherqui et al. show #StemCell transplants may also be promising therapeutic against #AlzheimersDisease. Cherqui Lab UCSD Sanford Stem Cell Institute La Jolla Institute Cell Reports doi.org/10.1016/j.celr… today.ucsd.edu/story/stem-cel…

Out now in Cell Reports, Dr. Stephanie Cherqui's (@Cherqui_S) lab shows hematopoietic #StemCell transplants can protect against memory loss, neuroinflammation and β-amyloid build-up in a mouse model of #AlzheimersDisease 🧠 today.ucsd.edu/story/stem-cel…

Backed by a $5M gift from Nancy & Geoffrey Stack Foundation, UC San Diego officially launches the Gene Therapy Initiative 🧬. Led by Drs. Cherqui & Muotri, the initiative will fuel research🔬+ gene therapies💉to benefit patients with #Genetics disorders today.ucsd.edu/story/uc-san-d…

Excited to be at the National MPS Society 37th Annual Family Conference to present some of my work at Cherqui Lab on gene modified HSPC for MPSIIIC! UC San Diego Health #GeneTherapy #StemCells

We are thrilled for our project scientist Anusha to be 1 of 10 researchers receiving a $20,000 grant from Uplifting Athletes! This grant will aid her research and support the 1 in 10 Americans diagnosed with a #RareDisease. upliftingathletes.org/2024/01/09/202…

Excited to kick off WORLDSymposia lysosomal disease conference this year by attending an important Cure Sanfilippo Fdn meeting on leveraging data to advance Sanfilippo therapeutic development! #lysosomes #genetherapy #hspc #sanfilippo #mps UC San Diego Health National MPS Society

Come checkout our Postdoc Veenita’s poster on Renal Fanconi Sundrome in Cystinosis WORLDSymposia

Check out this report from Cherqui Lab et al. "Rescue of Alzheimer's disease phenotype in a mouse model by transplantation of wild-type hematopoietic stem and progenitor cells", published in Cell Reports #ASGCT2024 hubs.li/Q02wFqBN0

California Institute for Regenerative Medicine is a proud sponsor of the Gene Therapy Initiative Symposium at UC San Diego Health, which bring together researchers and industry experts to share scientific discoveries and boost collaboration to advance cell and gene therapy treatments for patients everywhere. #gtiUCSD