Looking forward for the second day of the Clinical Trials in Gene Therapy UCSD Sanford Stem Cell Institute Cherqui Lab #genetherapy UC San Diego Health #clinicaltrials

Amazing couple of days at The Clinical Trial in Gene Therapy conference co-organised by Stephanie Cherqui Cherqui Lab at UCSD Sanford Stem Cell Institute! #genetherapy #clinicaltrials #lysosomaldisease #lysosomalstorage #LSDs Orchard Therapeutics - U.S. Sarepta Therapeutics

Este Jueves presentare mi investigación en Cherqui Lab sobre la terapia genética por trasplante de células madre hematopoyéticas para Mucopolisacaridosis en Academia Nacional de Medicina de Venezuela. Es un honor ser invitado a compartir mi investigación ante una audiencia tan prestigiosa en mi país.

I am looking forward to presenting my research in Cherqui Lab on Hematopoietic stem cell gene therapy for Mucopolysaccharidosis type IIIC at Academia Nacional de Medicina de Venezuela. It is an honour to be invited to share my research to such a prestigious audience in my home country.

I am very happy and grateful to have received the fellowship award from the Cure Sanfilippo Fdn to continue my work investigating the use of #stemcell #genetherapy to treat Sanfilippo type C in the Cherqui Lab UC San Diego Health

Excited to be back at WORLDSymposia and see the latest research on lysosomal diseases. Come check out my poster no. 35 in the Thursday afternoon session on my work Cherqui Lab on #stemcell #genetherapy for MPSIIIC. National MPS Society

Thank you Rafael A. Badell-Grau, PhD for representing our lab at WORLDSymposia 2023. Also, a special acknowledgement goes out to National MPS Society and Cure Sanfilippo Fdn for your fellowship supports!

Great to see my PI Prof. @Cherqui_S present her cystinosis Phase I/II clinical trial data. Cherqui Lab Cystinosis Research California Institute for Regenerative Medicine UC San Diego Health AVROBIO #clinicaltrials

Back at the #ASGCT annual meeting! Looking forward to all the exciting talks. ASGCT

Happy to be back presenting a poster at the ASGCT annual meeting on my work at Cherqui Lab on #stemcell #GeneTherapy for Sanfilippo C funded by National MPS Society & Cure Sanfilippo Fdn. Poster No. 649

Great week for the Cherqui lab ⁦ASGCT⁩ presenting our latest work! #stemcell #genetherapy ⁦UC San Diego Health⁩ linkedin.com/posts/stephani…

Honoured to have been awarded one of the ASGCT 2023 outstanding poster award for my abstract on my work in the Cherqui Lab UC San Diego Health on Hematopoeitic #stemcell #genetherapy for MPSIIIC funded by National MPS Society & Cure Sanfilippo Fdn

Congratulations to our #ASGCT23 Outstanding Poster Presentation Award recipients! Check out the abstracts behind the top 30 poster presentations at the 26th Annual Meeting. ow.ly/A34150OAR1O

Rafael Badell Madrid Excelente disertación sobre el Esequibo y sus soluciones . Gran oportunidad de recuperación pero quedan 9 meses . Última oportunidad. Libro : La Reclamación de Venezuela sobre el territorio Esequibo … será de lectura obligada. #ConsensoNacional #ATiempo Eduardo Rodriguez G.

Exciting article by my colleagues at the Cherqui Lab demonstrating further evidence of the potential use of #stemcell #GeneTherapy to treat neurodegenerative diseases! cell.com/cell-reports/f…

It was great to be able to present my work "Development of gene modified HSCT for Sanfilippo type C" at the #ADVANCE2023 meeting organised by the Cure Sanfilippo Fdn! #genetherapy #stemcells

Excited to be at the National MPS Society 37th Annual Family Conference to present some of my work at Cherqui Lab on gene modified HSPC for MPSIIIC! UC San Diego Health #GeneTherapy #StemCells

Excited to kick off WORLDSymposia lysosomal disease conference this year by attending an important Cure Sanfilippo Fdn meeting on leveraging data to advance Sanfilippo therapeutic development! #lysosomes #genetherapy #hspc #sanfilippo #mps UC San Diego Health National MPS Society

CIRM is proud to fund the incredible work that Don Kohn, MD, & his team at the UCLA Broad Stem Cell are doing to provide #stemcell treatments to patients with ADA-SCID, a rare immune deficiency disease that results in severe & recurrent infections that impact quality & length of life.