A novel approach to #genetherapy is improving lives in ways once thought impossible 🧬🧠
Bankiewicz Lab
go.osu.edu/CqBc
$SRPT 'As Luis and Manuela sighed in relief, they saw a new Lucas emerge.' 💪💪💪 #Elevidys #GeneTherapy #Duchenne #RareDisease Boston Children's Lucas receives gene therapy for DMD and finds his super muscles answers.childrenshospital.org/dmd-gene-thera…
Telomeres are markers of aging and guardians of genomic integrity.
This is why I took gene therapy to extend mine.
pulse.ly/upor8itce0
#bioviva #genetherapy #lizparrish #biohacking
Can our healthspan be hacked?
Thanks to pioneering research by BioViva, it might be within reach.
bioviva-science.medium.com/hacking-health…
#bioviva #genetherapy #lizparrish
Congrats to the team Pfizer Inc. for FDA approval of #AAV #GeneTherapy Beqvez for Hemophilia B 🎉
investors.pfizer.com/Investors/News…
The FDA approval of #Beqvez is another milestone in #hemophilia and #genetherapy .
Like #Hemgenix , this #AAV vector uses the hyperactive FIX-Padua.
I wrote about the widespread adoption of FIX-Padua:
cell.com/molecular-ther…
Also, detailed tweetorial:
twitter.com/DrSamelsonJone…
The Livestrong fertility assistance program is a blessing for young patients undergoing chemotherapy.
It's disappointing they will not extend the program to help preserve fertility in #SickleCell patients receiving gene therapy.
AllianceForFP Oncofertility Vertex Pharmaceuticals