Interview with Becky Quick x Scott Gottlieb, MD 🇺🇸: > [B. Quick]: "Let me ask you about natural history studies, because that's a huge issue in these communities... in some cases, it's just not ethical to be asking these patients to go through a double-blind study... are natural

Yes, DesertDweller_ROAR_4_A_CURE_4_HD — you can obtain them through a FOIA request. But the better path would be for Senator Ron Johnson to obtain them through his role as Chairman of the PSI. They have subpoena power. — $QURE #FDA

Here’s how anyone can submit a FOIA in ~2 minutes, in 3 steps... If you care about transparency on FDA decisions and gene therapies like $QURE AMT-130, submit one now. Let’s make these Arnold Ventures meetings public: [Step 1]: > Click → "Request Form" on this page:

Mike is right. The Huntington's community is small, but mighty. The work Lauren Holder is doing is incredible & inspiring. We all need to help her. $QURE #FDA — Kirsten Gillibrand | Evan Lukaske Rick Scott | Clare Lattanze Senator Ron Johnson | Grace Carnathan Rep. Jake Auchincloss 🟧 |

Based on publicly available info, there appear to be zero links between Houman David Hemmati, MD, PhD and Arnold Ventures. Companies he's been affiliated with have overlapped as conference sponsors with AV — but that seems to be it. That alone is a good start. Maybe that means he will act in

Hey Andrew Nixon — care to respond to Rachel Reising’s article? She wrote it from the depths of the swamp. Sincerely, #1 Fan of the Mosquito Fan Club $QURE U.S. FDA #FDA lansingstatejournal.com/story/opinion/…

Excellent piece by Peter Mantas on the path forward for $QURE AMT-130. Anyone stepping into a senior role (at any kind of organization) wants to establish themselves with quick, impactful wins. This is the mother of all quick, impactful wins: > A win for patients. > A win for

I don’t expect you to respond to this, Dr. Hemmati — but I hope you see this and know that under the previous CBER Director, what you’ve described (“But our health must remain above politics and political influence.”), is *exactly* what’s happened. — $QURE $XBI #FDA