Sports_Bios v well said - and if data are so compelling, the doc/pt community will be there primed to enroll in a confirmatory study - $BIIB is wasting time already w/this garbage, follow scientific rigor and answer whether this is legit or not vs trying to leverage a desperate community

Do you know an ASGCT member who has supported the translation of #GeneTherapy and #CellTherapy from preclinical to clinical research settings? Submit a nomination for the inaugural Jerry Mendell award. bit.ly/2PEUiEw

.U.S. FDA is committed to providing regulatory flexibility and guidance during this crisis, while fulfilling its duty to ensure products are safe and effective.

5/ Now everyone in the world is fighting for their lives with little hope, no cure, and no guarantee of survival—all while suffering financial hardship. Reassurance is now doctors saying there’s nothing they can do. Now the world knows what it’s like to be rare disease patient.

Joshua Potash Need tshirts & billboards:

This sums up all that people want... good cops stand up (or kneel down) - we need you to be the driving force of the movement to protect each other...

Our SVP of Global Policy, Government and Patient Affairs, Diane Berry, was recently interviewed on the Patients Rising podcast, discussing the 21st Century Cures Act.

$SRPT - So much love for Sandy - we will truly miss him but his legacy will remain all will always be part of the fabric of Sarepta...

$SRPT

Turns out they had the wrong guy, but he was still arrested for resisting arrest!

"There are challenges, but it's up to you to grasp them and turn them into opportunities." Hear from Vineet S. about what makes SRPT unique: bit.ly/3ninxLx

A 'must-see' enjoyable session by STAT Matthew Herper w/ four former FDA Commissioners Scott Gottlieb, MD 🇺🇸, @califf001, Hamburg & Henney with informal engaging banter & insights you never get while they are with the Agency! Also strong statement of support for Dr. Janet Woodcock!

I’ve watched the video 100 times now and I’m still in awe. Further, how the woman just walks by like this is normal.

.MACPAC excellent Partnership to Fight Chronic Disease (PFCD) must-read in AJMC shows why you should VOTE NO on ICER's harmful idea to modify MDRP for FDA accelerated approval drugs. #SupportPatients #MakeGoodChoices ajmc.com/view/limiting-…

BrightFarms is recalling packaged salad greens produced in its Rochelle, IL greenhouse farm because it has the potential to be contaminated with Salmonella. Consumers, restaurants, and retailers should not eat, sell or serve the affected products: go.usa.gov/xFcee

$AXSM the principal reasons given in the CRL relate to CMC considerations. The CRL identified the need for additional CMC data pertaining to the drug product and manufacturing process.

Excited to announce the close of our Series C #financing as we rewrite the rules of drug creation, advance our pipeline toward the clinic, and continue to grow our team! cellarity.com/news/cellarity… Flagship Pioneering #biotech #Boston #AI #machinelearning #drugcreation

Prescience Point Capital $LAZR could talk bullish points for hours, maybe days😁😎😉

The Delta in flight trivia game was awesome, is there an App to play at home?