Quick summary of $PRME July 2025 presentation 👇🏻:
• $PRME is shifting from platform validation to imminent clinical trials.
• The first ever human data (program PM359 for CGD) confirmed prime editing is safe and effective in humans.
• Lead liver programs:
-Wilson’s Disease
This weekend, members from our #ATTR team will be at the #ESCCongress. HCPs: Don’t miss our symposium on Monday, chaired by Dr. Julian Gillmore, discussing all things #amyloidosis and advancements in the field.
#ESCCongress #WCCardio
Magnitude 2, the pivotal Ph. 3 for ATTR-PN from $NTLA, added one new site in Argentina today.
Up to 15 sites which should go fast considering only 50 are needed.
Sites per country
3 in Argentina 🇦🇷
1 in Australia 🇦🇺
4 in Brazil 🇧🇷
1 in New Zealand 🇳🇿
2 in Singapore 🇸🇬
3 in
Enrollment completed in 3 months $NTLA
“Observers of the field said they’ve never seen that level of interest other than the very first time the first therapies were offered to these patients years ago.” 👀
“In a single month, 41 patients presented themselves to be screened.”
A single dose of a new cancer drug made a brain tumor almost disappear – in just five days.
Doctors at Massachusetts General Hospital reported “dramatic and rapid” tumor regression in the first patients treated with a next-generation form of CAR T-cell therapy for glioblastoma,