Nat Fabry Diseas Fdn
@fabrydisease1
Our primary goal is to provide education and support to enable people with Fabry disease to live better and longer lives. @jerrywalter
ID: 73217499
http://www.fabrydisease.org 10-09-2009 20:52:29
462 Tweet
746 Followers
48 Following
The Ellen Show
@theellenshow
The home for The Ellen DeGeneres Show on X. Enjoy the best moments from 19 incredible seasons!
Oprah Winfrey
@oprah
Rare Disease Day
@rarediseaseday
29 February 2024 is Rare Disease Day. Raising awareness for patients, families and carers around the world that are affected by rare diseases. #RareDiseaseDay
Lisa Morrise
@lisamorrise
Mom, Broadcaster, Professor, Exec Dir Consumers Advancing Pt Safety. NCQA CPC member. Patient Engagement. Love my dog & travel.
Rare Diseases
@checkorphan
CheckOrphan is the leading #news and information platform dedicated to #rarediseases and #orphandrugs
Fabry Disease News
@fabryalerts
Fabry Disease news, alerts, articles, etc.
Bill Gates
@billgates
Sharing things I'm learning through my foundation work and other interests.
National Organization for Rare Disorders (NORD)
@rarediseases
National Organization for Rare Disorders (#NORD) is the voice of the U.S. #RareDisease community for 40+ years strong. Official U.S. sponsor of #RareDiseaseDay.
Global Genes
@globalgenes
Empowering the Next Generation Rare Disease Advocate. Merged with RARE-X Dec. 2022. #CareAboutRare
EveryLife Foundation
@everylifeorg
Nonprofit org. dedicated to advancing the development of treatment & diagnostic opportunities for rare disease patients through science-driven public policy.
National MPS Society
@mpssociety
The National MPS Society exists to find cures for MPS and ML.
Accessia Health
@accessiahealth
Accessia Health is a leader in nonprofit #patientassistance for people with rare and chronic health conditions. We speak health and human.
Diplomat Specialty Infusion Group
@dploinfusion
We’ve moved. Please follow us @Optum. For customer care tweet @Optum_Support.
Sanofi US
@sanofius
We chase the miracles of science to improve people's lives. For U.S. residents only. Interactions on this page must comply with Sanofi US terms: bit.ly/US-terms
RareShare
@rareshareorg
RareShare is a social platform building communities for patients, families, and healthcare professionals affected by rare medical disorders.
Rare Diseases Clinical Research Network
@rarediseasesnet
NIH-funded network fostering collaborative research among 20 teams of researchers, patients, and clinicians, each focused on a group of rare diseases.
Beyond the Diagnosis
@beyondthedx
Beyond the Diagnosis unites art and science to raise awareness for children living with life-altering diseases.
uniQure
@uniqure_nv
uniQure is delivering on the promise of gene therapy - single treatments with potentially curative result for patients with severe genetic diseases.
MPS Society UK, here for those with rare diseases
@mpssocietyuk
MPS Society UK is the only registered charity providing professional support to those affected by MPS, Fabry and related diseases.
Fabry, Australia
@fabryaustralia
Fabry Australia is an incorporated patient organisation founded in 1994 by patients diagnosed with a rare genetic condition called Fabry Disease.
Frank Giustra
@frank_giustra
Dad #philanthropist Co-chair of @CrisisGroup blogger frankgiustra.com founder @acceso_org @modfarm @domenica_fiore @tbirdent @GiustraFdn
ASGCT
@asgctherapy
Advancing knowledge, awareness, and education leading to the discovery and clinical application of genetic and cellular therapies to alleviate human disease.
Fabry Support
@fabrydisease2
An account made for anyone with an interest in Fabry Disease. To share information and experiences, ask questions and raise awareness!!
Fabry International Network
@fabryintnetwork
FIN is an independent & vibrant network of Fabry patient associations whose purpose is to collaborate, communicate, promote best practices & empower patients
FSIG
@fabryorg
Increasing awareness for those with Fabry disease to create a brighter future, and better lives today - Education, Support, Awareness and Advocacy
Beacon Therapeutics
@beacontx_
Beacon Therapeutics is an ophthalmic gene therapy company founded to restore and improve the vision of patients with retinal diseases that result in blindness
Baebies
@baebiesinc
Our mission is to save lives and make lives better for all by bringing new technologies, new tests, and new hope. Everyone deserves a healthy start.
WORLDSymposia
@worldsymposia
We're Organizing Research on Lysosomal Diseases
Amicus Therapeutics
@amicusrx1
We are a global biotech company focused on discovering, developing & delivering high-quality medicines for people living with rare diseases.
CRISPR Therapeutics
@crisprtx
Canadian Fabry Assoc
@cdnfabry
Cell & Gene Therapy
@cgt_insights
OA journal from BioInsights; Senior Editor: Prof. Chris Mason, AvroBio & UCL. Register to read all content free of charge.
4DMT
@4dmolecular
Developing the best Adeno-Associated Vectors to meet unmet needs and unlock the true potential of gene therapy space. Check us out at 4DMT.com
STAT
@statnews
Reporting from the frontiers of health & medicine. Sign up for any of our 10 free newsletters here: statnews.com/signup
ThinkGenetic, Inc.
@thinkgenetic
Finding individuals in need of a diagnosis. Supporting pharma, research institutions, and healthcare systems. #RareDisease #ai
FSIGN
@fsign_2001
Fabry Support & Informatie Groep Nederland is een onhafhankelijke patiëntenvereniging voor mensen met de ziekte van Fabry
Chiesi Global Rare Diseases
@chiesigrd
We are making a rare difference.
Giustra Foundation
@giustrafdn
Founded in 1997 by businessman Frank Giustra, the Foundation supports a variety of causes focusing on children, education, economic development & homelessness.
The Journal of Inherited Metabolic Disease
@jimd_editors
At a recent Council meeting a decision was made that the SSIEM will no longer interact with X. Please find us on any other Social Media channel.
Rare2Aware
@rare2aware
#RareDisease awareness initiative by Takeda. For an audience outside the US and the UK. Contact us via DM. Community guidelines: bit.ly/2UIcdue
Sabina Kineen
@sabkin12
Trying my best to love, help, & respect others in this crazy world. #RareDisease #PatientVoice #FabryDisease #EhlersDanlos #MentalHealth #HealthEquity
Sangamo Therapeutics
@sangamotx
Committed to translating our ground-breaking science into genomic medicines that transform patients’ lives.
CheckRare
@checkrare
Leading publisher and learning platform focused on rare diseases. Rare Diseases Are Our Focus, Expertise, and Passion.
Idorsia
@idorsia
The purpose of Idorsia is to discover, develop and bring more, innovative medicines to patients. See our community guidelines: bit.ly/3gtrhr7
AllStripes
@_allstripes
Our mission is to unlock new treatments for people affected by rare disease.🚀
Remember The Girls
@remember_girls
Nonprofit organization aiming to break the stigma facing females impacted by X-linked conditions. #NotJustCarriers
Lysosomal&Rare Disorders Research&Treatment Center
@ldrtc_usa
#LDRTC is a #NonprofitOrganization with a vision to provide high quality care for patients and families with #LysosomalStorageDisorders and other #RareDiseases
My Fabry Disease
@myfabrydisease
Having Fabry Disease has a huge impact. It's amazing how few people, including medics, know about it, or understand how it affects people. Let’s change that.