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Delighted to co-host the new Research Topic "Genome and Transcriptome Editing to Understand and Treat Neuromuscular Diseases" with Rika Maruyama, Ph.D. Alyson Fiorillo, PhD Christopher Heier and Dr. Duan in Frontiers in Genome Editing Frontiers in Genome Editing frontiersin.org/research-topic… #CRISPR

50 free copies of our article are available below!: Restoration of dystrophin expression and correction of #Duchenne muscular dystrophy by genome editing tandfonline.com/doi/full/10.10… Taylor & Francis Research Insights UAlberta Med & Dent #CRISPR

This. If I had continued in the cure mindset for my son’s Duchenne diagnosis, I would have wasted 7.5 years of his life so far being unhappy. Accept and adapt. Let it go. Move forward. Smile. #Duchenne #DMD #Disability

Together with Isabelle Richard GENETHON France we describe a mouse model that mimics #LGMD2L muscle symptoms, offers insights into the basis of this disease, and test potential therapies content.iospress.com/articles/journ….

First R01 is being reviewed (or not reviewed) in study section today. It's totally normal to refresh my ERAcommons every hour, right?😬

A new study, co-authored by Elsevier's Bahar: mstdn.social/@bahar et al. reveals the #gendergap got wider, while paper submissions grew at the start of the #COVID19 pandemic: spkl.io/60184Ovtm #genderinresearch #researchworkforce #WomenInSTEM Flaminio Squazzoni Università degli Studi di Milano PLOS One

A pleasure to see that the Journal of Neuromuscular Diseases special issue celebrating Terry Partridge’s contributions to muscle research and mentorship is out. content.iospress.com/journals/journ… Thanks Raju for co-editing, Lochmüller Lab, Professor Jenny Morgan, Carsten and JND team for help and Pete Zammit for👇

Interesting new nature paper. MicroRNA sequence codes for small extracellular vesicle release and cellular retention. 🤯 tinyurl.com/mr3zzfzv

Harry's review article "Casimersen for Duchenne muscular dystrophy" is featured in the latest issue of #DrugsofToday Clarivate, summarizing the preclinical and clinical data currently available for casimersen, emphasizing pharmacokinetics and safety. Women & Children's Health Research Institute UAlberta Med & Dent

With our publication in Nature Medicine on pandemic-related barriers to the success of women in research, I’d like to shine a spotlight on gender equity for women physician-scientists, who face cumulative barriers imposed in medicine AND science rdcu.be/cHd4a 1/n

Hey #ScienceTwitter; is there a circRNA array/sequencing company/platform that you recommend? And are there any companies out there that synthesize custom cirRNAs?

I am so excited to share our newly published work on generating and characterizing the first mouse model of #Beckermusculardystrophy Christopher Heier The Heier Laboratory Nikki McCormack Edgewise Therapeutics FiorilloLab #duchennemusculardystrophy #dystrophin doi.org/10.1002/jcsm.1…

Test your muscular dystrophy knowledge: Which muscles are sick and how do you know? #MedEd #MedTwitter

Our new paper is out! Vamorolone improves disease and increases dystrophin in our Becker muscular dystrophy model. Now in clinical trials (NCT05166109) #MuscularDystrophy #Becker #dystrophin FiorilloLab Muscular Dystrophy Association Parent Project Muscular Dystrophy (PPMD) NIH NHLBI iScience journal cell.com/iscience/fullt…