
Thomas Leland
@tom1eland
PhD candidate in gene therapy center @ UMass Chan GSBS
ID: 1171895132142080001
11-09-2019 21:19:54
72 Tweet
83 Takipçi
244 Takip Edilen






Airplane seat assignment leads to in-person visit between UMass Chan Medical School gene therapy researchers and Italian family whose toddler daughter received AA9 vector for Canavan disease in clinical trial: direc.to/myem #RareDiseases #RareDiseases #CanavanDisease BridgeBio Pharma


Four-year-old Noa Greenwood, the third child to receive a promising gene therapy developed by researchers at UMass Chan Medical School, is an inspiration for families facing Canavan disease. Her story is part of our #RareDiseasesRealStories #podcast: direc.to/mrHf #RareDiseases
