New episode LIVE! This week, Stan interviews Sonja and Dr. Neil Shneider of Columbia Vagelos College of Physicians & Surgeons as they discuss Anna’s story – a girl fighting a fatal form of ALS. Stream here: ow.ly/klf750Kx3yM #nlorem #ALS #treatment #columbiaMed #podcast

ICYMI: Our latest podcast, Anna's Story of Hope and Help, is live! Join us in conversation with Dr. Stanley Crooke every other week and let us know what you think! Stream here: bxic0opcuyybbvdhptika2.captivate.fm/listen #nlorem #ALS #treatment #columbiaMed #podcast

Happy Friday! n-Lorem will be at the Global Genes Rare Patient Advocacy Summit next week. If you’re there in person come say hi to us at our booth! You can register online using the link in our bio. #rarepatientadvocacy #globalgenes #careaboutrare #supportnanorare #GGSummit

Our 2nd #lecture, by Stanley Crooke, M.D., Ph.D. (n-Lorem Foundation), of our series on #Innovations on #RareDisease is avaliable now for free. Discover solutions for patients living with Ultra Rare Diseases. fondation-ipsen.org/mooc/rare-dise…

This latest PEP episode is brought to you by Argonaut! This week, Dr. Crooke explains our approach to antisense – the highly efficient experimental technology used to best deliver on the needs of our patients. Stream here: ow.ly/JCl650KOsaH #sciencepodcast #drugdiscovery

Two drug discovery titans - and past rivals 🔥 - come together for the common cause of serving the nano-rare community. Stan is joined by John Maraganore 🇺🇸🇬🇷🇺🇦🇮🇱 on this episode of the Patient Empowerment Program. Listen: ow.ly/xX7q50L1u1v

Great to spend time with ⁦Stanley Crooke, M.D., Ph.D.⁩ on Henri Termeer Square today! ~150 years of biotech history in this picture!

Susannah, a nano-rare child, receives personalized medicine with the hopes to halt her neurodegenerative disorder. Her experimental medicine was created by n-Lorem to address her unique genetic mutation; the ultimate in personalized medicine. NYT exclusive linktr.ee/nlorem

Go n-Lorem, it's your birthday! Today marks three years of the n-Lorem Foundation providing hope and potential help to nano-rare patients and their families. We’ve received more than 160 applications for treatment and have accepted more than 80 patients.

All smiles and full of color here at n-Lorem as we light up our building and join the Global Chain of Lights on #RareDiseaseDay. #LightUpForRare National Organization for Rare Disorders (NORD) Rare Disease Day

We care about rare! Here are some highlights from last night's Global Chain of Lights event at n-Lorem. #RareDiseaseDay #LightUpForRare National Organization for Rare Disorders (NORD) Rare Disease Day

A way forward for diagnosis of patients with extremely rare genetic mutations go.nature.com/3XV03Qa

In this paper, I outline areas of reform that could couple the advances in health care technology with an integrated approach to address nano-rare patients and enable precision medicine treatment options.

On Thursday, July 27th, n-Lorem Chief Operating Officer, Sarah Glass, joins this panel of experts to discuss financing medicines for nano and ultra-rare conditions. This Endpoints News Webinar is FREE. Register TODAY! webinars.endpts.com/pharma-can-tar…

We're a little more than halfway through our biggest year yet and are thrilled to provide an update on our progress to treat as many people living with nano-rare diseases as possible. This is n-Lorem by the numbers.

Hope is possible. While the odds of an ASO created for a single person having the ability to be used as treatment for another are minimal, they are not zero. USA Today details this incredible story. usatoday.com/story/news/hea…

The 2023 End-year Chairman's Letter is now available: nlorem.org/our-approach/c… In this letter, Stanley Crooke addresses all and delivers a summary of n-Lorem's 2023 highlights and shares valuable insights and updates as the Foundation heads into 2024 with strong momentum.

n-Lorem marked a momentous milestone with the #GrandOpening of a new laboratory in San Diego’s biotech hub, Sorrento Valley. A ribbon-cutting ceremony commemorated the facility, which offers expanded lab and office space to meet the needs of our growing patient program pipeline.

Personalized antisense oligonucleotides ‘for free, for life’ — the n-Lorem Foundation. A recent correspondence from Joseph G. Gleeson Stanley Crooke, M.D., Ph.D. and colleagues n-Lorem Foundation #RareDiseaseDay nature.com/articles/s4159…

Happy #RareDiseaseDay! Today marks a crucial moment for raising awareness and advocating for change for the over 300M individuals worldwide living with rare diseases. Join us in showing support by wearing stripes in honor of Rare Disease Day!