5 ways gene therapy is helping change �' and save �' lives - Lifestyle from Xposé - Virgin Media Television virginmediatelevision.ie/xpose/article/…

Huge thanks to Medical Research Council for the translational funding that helped develop this #GeneTherapy for #ADASCID at UCL Great Ormond Street Institute of Child Health and Great Ormond Street Hospital for Children Couldn’t have done it without this funding....thank you!

Here is Prof. Bobby Gaspar, @Angy__Fa and the amazing team at Orchard Therapeutics - U.S. celebrating #JeanForGenes Day! Thank you so much for all your support and fantastic fundraising efforts! 👖💙🧬

Continue the great work #JeansForGenes helping people with genetic disorders!

The PID medical and scientific community has come an incredibly long way since the 70s and 80s. And this young man made huge contributions and sacrifices to help us understand more.

Delighted to be talking about #genetherapy for #SCID and other disorders. Thank you RARE Revolution Magazine for featuring this

#IPIC2019 is just around the corner! Learn more about how to get around Madrid and don't forget to register to the congress dinner. on Nov 7. If you still haven't registered to the congress just pack your bags and register onsite! ¡hasta pronto! mailchi.mp/ipopi/around-t…

Delighted to be talking at #IPIC2019 and supporting this important meeting #PID #SCID Thank you for the invitation!

Again and again emily m is forensic, to the point and totally brilliant! Regardless of labour, conservative or #PrinceAndrewInterview , it’s just about getting to the truth

In honor of the 1st #WorldSanfilippoDay last Saturday, we were privileged to host a mother of 2 Sanfilippo Syndrome (aka MPS-IIIA) children today as she walked us through her family’s journey. Learn more about Sanfilippo Syndrome from families it affects: bit.ly/2qvGqTE

⁦Prof. Bobby Gaspar⁩ sketches out the areas where #GeneTherapy is being used in #Paediatrics #GOSHConf2017 ⁦GOSH International⁩

Thank you for the invitation and great to be part of this meeting #GOSHconf19 talking about #GeneTherapy

A huge congratulations to Nizar Mahlaoui M.D., M.P.H., Ph.D. for receiving on behalf of Necker Hospital the prestigious Prix Galien Award in the category “Patient follow up care” for the Transition Care programme he established at Necker Hospital called “La Suite Necker”. So proud!

This is such promising and positive news for the CGD community. #ThursdayThoughts #cgd #stemcell Jeffrey Modell Foundation (JMF) thank you for sharing!

Orchard co-founder and gene therapy pioneer, Prof. Adrian Thrasher, MD, PhD, joined the Orchard team (virtually) today in honor of Orchard’s 5-year anniversary. Thank you for sharing your stories from the early days of gene therapy, including your work with our CEO Prof. Bobby Gaspar!

Catch this fascinating chat from #RAREfest20. Georgina of Archangel MLD Trust & Prof. Bobby Gaspar of Orchard Therapeutics - U.S. discuss the hope that #GeneTherapy for rare single-gene disorders brings & their campaign for comprehensive newborn screening in the UK.  Watch here bit.ly/2KlCkqH

.Prof. Bobby Gaspar Orchard Therapeutics - U.S. discusses the company’s sharpened focus, its gene therapy in development for metachromatic leukodystrophy, and where he sees the greatest opportunities for Orchard going forward. Global Genes #RARECast #genetherapy globalgenes.org/rare-cast/epis…

Well done Clara Gaspar ...v important and brave story

Libmedly: World's 'most expensive' drug recommended for NHS use bbc.co.uk/news/health-60…