INPDA International Niemann-Pick Disease Alliance Secretary, and Niemann-Pick UK Chief Executive Toni Mathieson was honoured to be in attendance at the Niemann-Pick Type C Patient-Focused Drug Development in... facebook.com/inpda.org/post…

Niemann-Pick Type C Externally-led Patient-Focused Drug Development Meeting (video stream now available!) The Niemann-Pick Type C (NPC) externally led Patient-Focused Drug Development (PFDD) meeting is a groundbreaking initiative... youtube.com/watch?v=iHcDkd…

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Less than SIX months to go until INPDA founding member group Niemann-Pick UK's Annual Family Conference & Interactive Workshop on Niemann-Pick Disease(s)! facebook.com/inpda.org/post…

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In the following video Helenida Tauil reports from the Associação Niemann-Pick Brasil's 1st Symposium on Rare Diseases in Londrina For further information on INPDA International Niemann-Pick Disease Alliance member group ANPB,... youtube.com/watch?v=2cDqbY…

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“NNPDF Industry Update Webinar Series featuring Intrabio” INPDA International Niemann-Pick Disease Alliance member group the National Niemann-Pick Disease Foundation, Inc.'s Industry Update Webinar Series will continue on the... nnpdf.org/news-media/nnp…

We need YOUR help! ❤️ Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazymesur…

We need YOUR help! ❤️ Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazymesur…

We need YOUR help! ❤️ Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance Orphazyme is investigating is called arimoclomol citrate, which is... surveymonkey.com/r/orphazymesur…

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We need YOUR help! ❤️ Orphazyme is working to create a new therapeutic approach to treat Niemann-Pick disease Type C. The name of the active substance... surveymonkey.com/r/orphazymesur…

Chris Andrews, Father to Abby and Belle, two children with Niemann-Pick disease type C, shares his story with those in attendance at last month's Niemann-Pick Type C Disease Patient-Focused Drug Development Meeting. To learn more... youtube.com/watch?v=Gfh8A7…

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