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Explore fetal precision medicine: prenatal genomic sequencing & in-utero therapies for genetic diseases at #SMFM25 course, Maternal Fetal Precision Medicine. Register at smfm.org/2025 Teresa Sparks

Congratulations to Center Co-Director Dr. Mary Norton on receiving the prestigious SMFM Lifetime Achievement Award! Honoring her leadership, advocacy, research, and dedication to maternal-fetal medicine. Well deserved! #SMFM #MaternalFetalMedicine #LifetimeAchievement

Join us at #WORLDSymposium for interim results from the UC San Francisco #PEARLTrial—a first-in-human Phase 1 trial of In Utero #EnzymeReplacementTherapy for Lysosomal Disorders (PI Tippi MacKenzie). Presented by BillieLianoglou Thurs, Feb 6 @ 8:30am #WORLDSymposia pearltrial.ucsf.edu

Honoring #RareDiseaseDay and the strength of the #rare community. Your voices drive progress, and together, we’re working toward better treatments. #RareDiseaseAwareness #PEARLTrial pearltrial.ucsf.edu

Register now for "Empowering Patients 2025: A Cell and Gene Therapies Summit" on March 12–13, hosted by ASGCT! This free, virtual event in two half-day sessions offers educational discussions for foundation leaders, patients, and caregivers to better understand

Attending #ACMGMtg25? Learn about the latest advances and clinical findings at our poster presentations and Learning Lounge on Thursday, March 20. We hope to connect with you in LA! #PEARLTrial @billielianolgou

Happening now at #ACMGMtg25: Poster presentations (authors present at odd-numbered posters), 10:30 AM – 12:00 PM. LACC, Exhibit Hall DE. Go see some amazing #medicalgenetics research!

Please RT! Applications are due June 1 for this special research fellowship in #FetalDiagnosis and #FetalTherapy. Experience our vibrant training program, mentorship, multidisciplinary collaboration, and cutting-edge fetal diagnostics and therapies. tiny.ucsf.edu/15AQrW

April 15 is #InternationalPompeDay. We stand with the #Pompe community and are grateful for enrolling 3 #IOPD patients in our prenatal ERT #PEARLTrial. We're excited by the positive impact, as seen in the story of the first family receiving the protocol: bit.ly/3Mb9uqg

#Crouchlab and friends and family at the UCSF Center for Maternal-Fetal Precision Medicine 10 year anniversary celebration 🍾 🎉thrilled to be a part of this #visionary group now w/#clinicaltrials for #inutero therapies. Let’s go for it, for children’s future health 👶🏻👧🏾🧒🏼UCSF Pediatrics Neo Kids On The Block UCSF Broad Stem Cell

10 years and counting. These are a few of the many remarkable people who contribute to the ambitious vision of our Center co-directors, Mary Norton and Tippi MacKenzie:  A world where all children are born healthy.

Hear how gene therapies can address serious genetic diseases before birth. @MacKenzieTippi will deliver a George Stamatoyannopoulos Memorial Lecture at the @ASGCT Annual Meeting on May 15.  #ASGCT2025 #GeneTherapy #PrenatalResearch #raredisease

Intra-amniotic ASO treatment improves phenotypes in preclinical SMA models, suggesting a promising, minimally invasive prenatal approach for SMA and other early-onset neurological disorders. @MacKenzieTippi lab, UC San Francisco, @UCDavis, Johns Hopkins Medicine bit.ly/4jV38tL

SEMINAR: Please join us on 6/12, 8am PDT, when Dr. Evangelia Vlachodimitropoulou from King’s College Hospital, will present “In Utero Transfusions (IUT) Beyond 35 Weeks Gestation in Alpha #Thalassemia Major” REGISTER: tinyurl.com/ATM-Jun2025

On May 15 #MPSAwarenessDay, we stand with the #MPS community. We are deeply grateful to the families participating in the prenatal ERT #PEARLTrial UC San Francisco. Their courage and their contributions are humbling. Meet one of these inspiring families: bit.ly/3OgxCZD #ShineForMPS

Researchers have made a breakthrough in treating spinal muscular atrophy (SMA) before birth. Their innovative approach delivers a genetic therapy into amniotic fluid, & potentially opens a door to earlier, more effective treatments: STAT Megan Molteni bit.ly/STAT-SMA

‼️Join us Thurs, 5/29 for Getting to Patients as Dr. Michael Matthay presents groundbreaking research on bone marrow-derived stromal cells for ARDS—bridging pre-clinical science, clinical trials, and real patient experience. Moderated by Dr. Julia Brown 👇 tiny.ucsf.edu/StromalCellsAR…