Ana Mingorance
@cnsdrughunter
🧠 🧬 Neuroscientist. Looking for new medicines for CDKL5, SCN1A, SHANK3, DHPS and a few others.
ID: 358743576
http://draccon.com 20-08-2011 12:34:58
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With today's announcement from Encoded Therapeutics, the #Dravet trials with gene therapy ETX101 are: - Australia WAYFINDER: 4 kids ages 3-7 - USA ENDEAVOR: 4 kids under 3 (part 1) - UK EXPEDITION: 4 kids under 4 All to start in 2024 to measure safety, tolerability and efficacy signal.