Sarepta Therapeutics
@sarepta
Commercial-stage biopharma company focused on the discovery & development of precision genetic medicine to treat rare neuromuscular diseases. bit.ly/3XgXshH
ID: 2216555822
http://sarepta.com 26-11-2013 21:45:22
1,1K Tweet
5,5K Followers
62 Following
Nationwide Children's Hospital
@nationwidekids
Nationwide Children's Hospital, one of America's largest pediatric hospitals and an international leader in #research. A follow does not equal endorsement.Rare Disease Day
@rarediseaseday
29 February 2024 is Rare Disease Day. Raising awareness for patients, families and carers around the world that are affected by rare diseases. #RareDiseaseDayRoche
@roche
We advance science so that we all have more time with the people we love. Read our community guidelines: go.roche.com/CGMark Hagen
@mhagen02
EURORDIS-Rare Diseases Europe
@eurordis
An alliance of over 1,000 patient organisations working across borders and diseases to improve the lives of all people living with rare diseases.Kendall Square Association
@kendallnow
Your best resource for news & events in Kendall Square, Cambridge, MA.HBAnet
@hbanet
The Healthcare Businesswomen’s Association's purpose is to further the advancement and impact of women in the business of healthcare #HBAimpact #4genparityCureDuchenne
@cureduchenne
We are committed to improving the lives of those affected by Duchenne through accelerating research, improving care and empowering the community.Matthew Herper
@matthewherper
Writing and events at STAT. This is biology's century; Every data point has a face. ‘21 Polk Award. Mastodon: @[email protected]Forbes Health
@forbeshealth
For more on the business of big pharma, health care and science follow @ForbesScience, @Forbes.Parent Project Muscular Dystrophy (PPMD)
@parentprojectmd
Let's fight for every future. #PPMDeveryfuture #EndDuchenneMuscular Dystrophy Association
@mdaorg
MDA is the #1 voluntary health organization in the United States for people living with #MuscularDystrophy, #ALS, and related #neuromuscular diseases.MDA Advocacy
@mda_advocacy
MDA's Advocacy empowers the voice of the @MDAorg community & protects the interests of those we serve.American Academy of Neurology
@aanmember
The official account of the American Academy of Neurology.Genetic Counselors
@geneticcouns
National Society of Genetic Counselors (NSGC) is the leading voice, authority and advocate for the genetic counseling profession. RT does not equal endorsement.Alnylam Pharmaceuticals
@alnylam
Leader in #RNAiTherapeutics, having pioneered this innovative approach to silencing the genes that cause disease. Community guidelines: bit.ly/2FcRhJy.NORD
@rarediseases
National Organization for Rare Disorders (#NORD) is the voice of the #RareDisease community. Official US sponsor of #RareDiseaseDay.Global Genes
@globalgenes
Empowering the Next Generation Rare Disease Advocate Merged with RARE-X Dec. 2022. #CareAboutRareKathryn Bryant Knudson
@speakfoundation
Founder of the patient-led Speak Foundation NPO, Jesus follower, UVa grad, & rare disease advocate for Muscular Dystrophy! #believeforacureAldevron
@aldevron
We serve the biotech industry by manufacturing high quality biologics, impacting lives worldwide. 🔸Plasmid DNA 🔸mRNA 🔸Proteins Discovery➡Clinical➡CommercialMaria Sirois
@mariasirois
Maria Sirois, PsyD, psychologist, inspirational speaker, consultant, author. Positive psychology, happiness, authenticity, resilience, recovery from loss.CureCalpain3
@curecalpain3
C3 is a non-profit organization driving research to cure limb-girdle muscular dystrophy type 2A, also referred to as LGMD2A/R1 and CalpainopathyCanal District Kendall
@canaldistrictks
Canal District Kendall is a 10-acre, master-planned development. Live, Work, Shop, Play, Eat: Come see what we have to offer! #BioMedRealtyRareConnect
@rareconnect
🌐Connecting #raredisease patients globally at rareconnect.org. 💻Website help at @RareConnectSup.Fedica
@fedicahq
(Formerly Tweepsmap) Optimize, Visualize & Strategize With AI: All-in-One Social Media Publishing, Analytics, Listening & Analysis Platform.MASS AWIS
@massawis
The Association for Women in Science Massachusetts Chapter, championing the interests of women in science, technology, engineering and mathematics.HBA New England region
@hbanewengland
The HBA's core purpose is to further the advancement and impact of women in the business of healthcare.Women In Bio
@womeninbio
A 501(c)(3) nonprofit organization committed to promoting careers, leadership & entrepreneurship for all women in the life sciences. #womeninbioDr. Rodino-Klapac
@rodinoklapac
Dedicated scientist focused on developing gene therapy treatments for muscular dystrophyASGCT
@asgctherapy
Advancing knowledge, awareness, and education leading to the discovery and clinical application of genetic and cellular therapies to alleviate human disease.Team Joseph
@teamjosephinfo
Our mission is to fund research to find a cure for Duchenne muscular dystrophy and support families with immediate needs to help care for a child with Duchenne.Jett Foundation
@jettfoundation
Empowering families. Fighting Duchenne muscular dystrophy.reacHIRE
@reachire
Engage & retain female talent with the Aurora talent experience platform, & tap into new talent pools with Returnships. #talentexperience #returntoworkAll Wheels Up ♿✈
@allwheelsup
Working to increase awareness for safer and more dignified accessible travel through research and advocacy. Text FLY to 707070 to DonateWorld Duchenne Awareness Day 🎈
@duchenneday
Join us on September 7 on World Duchenne Awareness Day #WDAD2024. Help raise awareness for people living with dystrophinopathies!LGMD Awareness Foundation, Inc
@lgmdawareness
A 501(c)(3) advocacy organization dedicated to globally raising awareness of the rare neuromuscular diseases known as Limb-girdle muscular dystrophy (LGMD).WMS
@worldmusclesoc
We invite you to the 29th International Annual Congress of the World Muscle Society in 2024. This is the premier annual Congress on #neuromuscular disorders.Child Neurology Society
@childneurosoc
Child Neurology Society's official twitter account for members. At the #CNS, every member counts because every child counts. Retweets ≠ endorsement.Myonexus Therapeutics
@myonexustx
We are developing the first-ever corrective gene therapies for LGMD, debilitating rare diseases with no treatments or cure today.Project Onramp
@projectonramp
Project Onramp connects underserved college students in Massachusetts with paid internships in biotech, giving them a first step towards a rewarding career.Institute for Gene Therapies
@gene_therapies
Gene therapy is transforming how we treat diseases. But today’s healthcare system can’t realize its potential. We’re changing that.Institut de Myologie
@inst_myologie
Centre d'expertise sur le #muscle et ses pathologies créé par @telethon_france @Inserm @Sorbonne_Univ_ @APHP #myology #research #care #clinicaltrials #MNMThe Rare Disease Company Coalition
@rarecoalition
We are a coalition of life science companies committed to discovering, developing & delivering rare disease treatments for the patients we serve. #OneRareVoiceMrs Suvarna
@mrssuvarna91308
Cartesian Therapeutics
@cartesiantx
Clinical-stage company pioneering mRNA cell therapies for the treatment of autoimmune diseases.Women In Bio Boston Chapter
@wib_boston
John Maraganore 🇺🇦🇮🇱
@jmaraganore
Founding CEO of @Alnylam. Pioneered RNAi therapeutics as a whole new class of medicines for patients. Now bioentrepreneur-at-large. Opinions are my own.World Duchenne Organization
@worldduchenne
Global organization to find a cure and viable treatment for those lives affected by dystrophinopathies: Duchenne and Becker Muscular Dystrophy. RT ≠ endorsementGenEdit Inc
@genedit_inc
Dyno Therapeutics, Inc.
@dyno_tx
Dyno Therapeutics is a pioneer in applying artificial intelligence to gene therapy, focused on AAV capsid engineering. Join our startup: dynotx.com