REGENXBIO
@regenxbio
REGENXBIO is dedicated to transforming the lives of people suffering from severe diseases with significant unmet medical need through our NAV® gene therapy.
ID: 702977473710067712
http://www.regenxbio.com 25-02-2016 22:04:25
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Thank you to Foundation for FDA for bringing together stakeholders, including regulators, patient advocates and industry, to discuss the important role of biomarkers in developing new therapies for rare disease. Read the report about the unmet need for patients with neuronopathic MPS.
Our team was pleased to participate in CureDuchenne's family workshop in Minneapolis this past weekend. Heartfelt thanks to CureDuchenne for their commitment to supporting and educating the Duchenne community.
Today, we announced that we will be sharing data from our RGX-121 program for the treatment of MPS II, also known as Hunter syndrome, at the SSIEM 2024 Annual Symposium. Learn more: ir.regenxbio.com/news-releases/… #SSIEM2024
Yesterday we welcomed Katie Morgan and her son Andy, who lives with Duchenne, to REGENXBIO. Andy’s energy and enthusiasm brought smiles to everyone’s faces. We ended the day with a walk to support Parent Project Muscular Dystrophy (PPMD). Thank you, Katie and Andy, for spending the day with us!